Projects per year
- 1 - 50 out of 404 results
Search results
-
Active
Transforming treatment of inherited bone marrow failure in Fanconi anemia by in vivo precise genome editing
Moriarity, B. S., Wagner, J. E. & Webber, B. R.
FANCONI ANEMIA RESEARCH FUND, INC.
2/1/24 → 1/31/26
Project: Research project
-
Cancer Center Support Grant
Yee, D., Antonarakis, E., Beckman, K. B., Betts, B., Blaes, A. H., Eaton, A., Ellis, K. M., Felices, M., Geller, M. A., Ghebre, R. G., Griffin, T. J., Hallstrom, T. C., Harki, D. A., Hatsukami, D. K., Hirsch, B. A., Huang, R. S. S., Johnson, S., Juckett, M. B., Lange, C. A., Le, C. T., Luo, X., McKenna, D. H., Miller, J. S., Moriarity, B. S., Muretta, J. M., Murray, T., Nelson, H. H., Ondrey, F. G., Patel, M. R., Pennell, C. A., Petersen, A. J., Peterson, L. A., Poynter, J., Pratt, R. J., Sarver, A. L., Schendzielos, D. L., Schilz, A., Schwertfeger, K., Seelig, D., Shimizu, Y., Stepanov, I., Temiz, N. A., Ventz, S., Villalta, P. W., Vogel, R., Wagner, J. E., Wang, J., Webber, B. R., Weigel, B. J., Yamamoto, M. & Zhang, L.
NIH NATIONAL CANCER INSTITUTE (NCI)
2/1/24 → 1/31/29
Project: Research project
-
Mechanisms to redirect tumor associated macrophages to target retinoblastoma cells
Hallstrom, T. C., Chen, L. & Linden, M. A.
ALEX'S LEMONADE STAND FOUNDATION
9/15/23 → 9/15/25
Project: Research project
-
P300/CBP inactivation, a novel epigenetic therapeutical approach for Ewing sarcomas
Bosnakovski, D., Das, S. & Mills, L. J.
9/1/23 → 8/31/25
Project: Research project
-
National Adrenoleukodystrophy (ALD) Registry
Gupta, A. O., Lund, T. C. & Orchard, P. J.
ASSOC OF PUBLIC HEALTH LABORATORIES, US Dept. of Health & Human Services HRSA
9/1/23 → 6/30/24
Project: Research project
-
HMGB1 in EB-Associated Squamous Cell Carcinoma
Bui, K. G.
NIH NATIONAL CANCER INSTITUTE (NCI)
8/1/23 → 7/31/27
Project: Research project
-
Collection of Gene Mutations for Laboratory Quality Assurance: Newborn Screening Accuracy Project
SEQUOIA FOUNDATION, CENTERS FOR DISEASE CONTROL & PREVENTION
5/15/23 → 5/14/28
Project: Research project
-
Off-the-Shelf Immune Effector Cells for Hematological Malignancies
Wagner, J. E., Bachanova, V., Betts, B., Brunstein, C. G., Cichocki, F. M., De For, T. E., Eaton, A., Hippen, K. L., Luo, X., Maakaron, J., McKenna, D. H. & Tolar, J.
NIH NATIONAL CANCER INSTITUTE (NCI)
5/5/23 → 4/30/28
Project: Research project
-
A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects with Cerebral Adrenoleukodystrophy
3/23/23 → 3/31/28
Project: Research project
-
Project 2: Novel Approaches to Inducing Lung Allograft Tolerance in NHPs
MASSACHUSETTS GENERAL HOSPITAL, NIH Nat'l Inst of Allergy & Infect Dis
3/23/23 → 2/29/28
Project: Research project
-
Interrogation of mDUX expression in muscle in mice
FACIOSCAPAULOHUMERAL (FSH) SOCIETY
12/5/22 → 12/4/24
Project: Research project
-
REVEAL - Research Evaluating Vagal Excitation and Anatomical Linkages.
Osborn, J., Crawford, P., Darrow, D., Drawz, P. E., Dudley, S., Eberly, L., Fonkoue, I. T., Henry, T. R., Hering, B. J., Ikramuddin, S., Johnson, M. D., Keller-Ross, M. L., Lim, K. O., Lim, H. H., Loavenbruck, A. J., McCarty, C. A., Meyer, M., Mueller, B. A., Murray, T., Nahas, Z., Netoff, T. I., Panoskaltsis-Mortari, A., Park, M. C., Puchalska, P., Ramachandran, S., Singh, A., Talkachova, A., Tignanelli, C. J. & Walczak, T. S.
NATIONAL INSTITUTES OF HEALTH (NIH)
9/23/22 → 8/31/25
Project: Research project
-
To explore the molecular and cellular effects of transient DUX4 expression in skeletal muscle
Bosnakovski, D., Gearhart, M. D. & Magli, A.
NIH NIAMS NATL INST OF ARTHRIT
9/1/22 → 6/30/27
Project: Research project
-
Foundations for a Phase 1 clinical trial of cell-based therapy for Duchenne muscular dystrophy
Kang, P. B., Karachunski, P. I., Perlingeiro, R. & Wagner, J. E.
NIH NIAMS NATL INST OF ARTHRIT
7/15/22 → 6/30/24
Project: Research project
-
In Vivo Prevention of Murine GVHD
Blazar, B. R. & Panoskaltsis-Mortari, A.
NIH Nat'l Inst of Allergy & Infect Dis
7/1/22 → 6/30/27
Project: Research project
-
Engineered immune cells for safer and more effective tumor therapy
7/1/22 → 6/30/24
Project: Research project
-
Enhancing Treg Therapeutic Efficacy in GVHD
Blazar, B. R., Griffin, T. J., Hippen, K. L. & Osborn, M. J.
NIH NAT'L HEART, LUNG, AND BLOOD INSTITU
5/15/22 → 3/31/26
Project: Research project
-
A Phase I Open Label Study to Evaluate the Safety andTolerability of ISP-001 in Patients with MucopolysaccharidosisType I
12/9/21 → 1/1/26
Project: Research project
-
Dose Optimization of Nervonic Acid-a Potential Therapy to Alleviate Disease Progression in Adrenoleukodystrophy
NIH NAT'L CTR FOR ADVANCING TRAN SCIENCE
7/1/21 → 5/31/24
Project: Research project
-
Sensory Function and Chronic Pain in Cerebral Palsy
Symons, F. J., Erickson, D. J., Panoskaltsis-Mortari, A., Simone, D. A., Walk, D. & Wilcox, G. L.
NIH NAT'L INST OF CHILD HEALTH/HUMAN DEV
5/14/21 → 2/28/27
Project: Research project
-
Exploiting the VISTA Pathway to Prevent Acute GVHD and Control Steroid Refractory Disease
Blazar, B. R. & Noelle, R. J.
National Heart, Lung, and Blood Institute
2/15/21 → 1/31/25
Project: Research project
-
A Phase 3, Open-label, Single Arm, Multicenter Study of Ravulizumab in Addition to Best Supportive Care in Pediatric Participants (from 1 month to < 18 years of age) with Thrombotic Microangiopathy (TMA) after Hematopoietic Stem Cell Transplantation (HSC
Srikanthan, M. & Smith, A. R.
9/20/20 → 8/31/25
Project: Research project
-
Characterizing Innate Immune Dysregulation in Tonsils of Individuals with Down Syndrome
Verneris, M. R.
National Heart, Lung, and Blood Institute
9/18/20 → 3/31/25
Project: Research project
-
Skin-targeted Cell Therapy for Recessive Dystrophic Epidermolysis Bullosa
Tolar, J., Moriarity, B. S., Osborn, M. J. & Webber, B. R.
NIH NIAMS NATL INST OF ARTHRIT
9/1/20 → 8/31/25
Project: Research project
-
Probing the activity of DUX4 in FSHD
NIH NIAMS NATL INST OF ARTHRIT
8/18/20 → 7/31/25
Project: Research project
-
An Open Label Expanded Access Study of Omidubicel, for Allogeneic Transplantation in Patients with Hematological Malignancies
Wagner, J. E. & Brunstein, C. G.
4/23/20 → 4/30/25
Project: Research project
-
Engineered B Cells as a Universal Platform for the Treatment of Enzymopathies
Moriarity, B. S., Lund, T. C., McIvor, R. S., Orchard, P. J. & Webber, B. R.
NIH Nat'l Inst of Allergy & Infect Dis
3/1/20 → 2/28/25
Project: Research project
-
A phase II pilot trial to estimate survival after a non-total body irradiation (TBI) based conditioning regimen in patients diagnosed with B-acute lymphoblastic leukemia (ALL) who are pre-allogeneic hematopoietic cell transplantation (HCT) next-generatio
MacMillan, M. L. & Neglia, J. P.
CHILDREN'S HOSPITAL LOS ANGELES, GATEWAY FOR CANCER RES
2/1/20 → 1/31/25
Project: Research project
-
Lysosomal Disease Network
Whitley, C. B., Ahmed, A., Braunlin, E. A., Cortez, D., Eisengart, J., King, K. E., Nestrasil, I. & Orchard, P. J.
NIH NAT INST OF NEURO DISORDERS & STROKE
9/15/19 → 7/31/25
Project: Research project
-
A Phase 3 Study Evaluating Gene Therapy by Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo with the LentiGlobin BB305 Lentiviral Vector in Subjects with Sickle Cell Disease.
Gupta, A. O. & Smith, A. R.
9/1/19 → 7/31/24
Project: Research project
-
MT2019-09: A randomized trial of low versus moderate exposure busulfan for infants with severecombined immunodeficiency (SCID) receiving TCR????+/CD19+ depleted transplantation: A Phase II studyby the Primary Immune Deficiency Treatment Consortium (PID
Ebens, C. & Smith, A. R.
CHILDREN'S HOSPITAL LOS ANGELES, NIH Nat'l Inst of Allergy & Infect Dis
8/16/19 → 5/31/24
Project: Research project
-
Training in Lung Science
Wendt, C. H., Bitterman, P. B., Ingbar, D. H. & Panoskaltsis-Mortari, A.
NIH NAT'L HEART, LUNG, AND BLOOD INSTITU
8/1/19 → 7/31/24
Project: Research project