Projects per year
Search results
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Active
National Adrenoleukodystrophy (ALD) Registry
Gupta, A. O., Lund, T. C. & Orchard, P. J.
ASSOC OF PUBLIC HEALTH LABORATORIES, US Dept. of Health & Human Services HRSA
9/1/23 → 6/30/24
Project: Research project
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Collection of Gene Mutations for Laboratory Quality Assurance: Newborn Screening Accuracy Project
SEQUOIA FOUNDATION, CENTERS FOR DISEASE CONTROL & PREVENTION
5/15/23 → 5/14/28
Project: Research project
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A Phase 3 Study Evaluating Gene Therapy by Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo with the LentiGlobin BB305 Lentiviral Vector in Subjects with Sickle Cell Disease.
Gupta, A. O. & Smith, A. R.
9/1/19 → 7/31/24
Project: Research project
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Finished
Mucopolysaccharidosis Newborn Screening meeting
ASSOC OF PUBLIC HEALTH LABORATORIES, US Dept. of Health & Human Services HRSA
8/23/22 → 9/30/23
Project: Research project
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Collection of Gene Mutations for Laboratory Quality AssuranceNewborn Screening Accuracy Project
SEQUOIA FOUNDATION, CENTERS FOR DISEASE CONTROL & PREVENTION
5/12/22 → 10/14/23
Project: Research project
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National Adrenoleukodystrophy (ALD) Registry
ASSOC OF PUBLIC HEALTH LABORATORIES, HRSA MATERNAL AND CHILD HEALTH (MCH)
11/26/20 → 8/31/23
Project: Research project
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Long Term Outcomes in Mucopolysaccharidosis Type I-Hurler (MPS I-H) PatientsAfter Hematopoietic Stem Cell Transplantation (HSCT)
1/9/20 → 12/31/20
Project: Research project
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A Phase 3 Study of Lenti-D Drug Product After Myeloablative Conditioning Using Busulfan and Fludarabine in Subjects ≤ 17 Years of Age With Cerebral Adrenoleukodystrophy (CALD)
Orchard, P. J., Gupta, A. O., Kenney-Jung, D. L. & Lund, T. C.
2/1/19 → 1/31/24
Project: Research project