Medicine & Life Sciences
Mucopolysaccharidosis I
100%
Mucopolysaccharidoses
44%
Mucopolysaccharidosis II
37%
Iduronidase
36%
Mucopolysaccharidosis III
32%
Enzyme Replacement Therapy
31%
Mucopolysaccharidosis VI
23%
Glycosaminoglycans
20%
Iduronate Sulfatase
15%
Genetic Therapy
13%
Enzymes
12%
Gangliosidoses
12%
Child
11%
vestronidase alfa
10%
Phenotype
10%
Genes
9%
Mutation
8%
Mucopolysaccharidosis VII
8%
Lysosomal acid lipase deficiency
8%
Therapeutics
7%
GM1 Gangliosidosis
7%
Phenylketonurias
7%
Bone Marrow Transplantation
7%
Bioreactors
7%
Cell Transplantation
6%
Brain
6%
Lysosomal Storage Diseases
6%
Hematopoietic Stem Cell Transplantation
6%
GM2 Gangliosidosis
6%
N-Acetylgalactosamine-4-Sulfatase
6%
Hexosaminidases
6%
Gene Editing
5%
Liver
5%
Heparitin Sulfate
5%
Transgenes
5%
Safety
5%
Sandhoff Disease
5%
Glycogen Storage Disease Type II
5%
Placebos
5%
sapropterin
5%
Neonatal Screening
5%