Medicine & Life Sciences
Mucopolysaccharidosis I
100%
GM1 Gangliosidosis
96%
Gangliosidoses
73%
Gaucher Disease
65%
Iduronidase
58%
eliglustat
42%
Enzyme Replacement Therapy
39%
Glucosylceramidase
34%
chitotriosidase
34%
Mucopolysaccharidosis II
32%
Galactosidases
32%
GM2 Gangliosidosis
31%
Caregivers
30%
sapropterin
29%
Musculoskeletal Diseases
28%
TimeLine
27%
Phenylketonurias
27%
Adalimumab
26%
Gene Editing
26%
Symptom Assessment
24%
Pharmacogenetics
24%
Blood-Brain Barrier
24%
Standard of Care
23%
Therapeutics
22%
Enzymes
22%
Gyrus Cinguli
22%
Cardiovascular System
20%
Placebos
19%
Cell Transplantation
19%
Phenotype
19%
Glutamic Acid
18%
Biomarkers
17%
Safety
17%
Pharmacokinetics
17%
Parents
16%
Putamen
15%
Oxidative Stress
15%
Monoclonal Antibodies
15%
Genotype
15%
Pain
14%
Alleles
14%
Gangliosides
14%
White Matter
12%
Mutation
12%
Walking
12%
Magnetic Resonance Spectroscopy
11%
isospaglumic acid
11%
Phenylalanine Hydroxylase
11%
Longevity
11%
Clinical Trials
11%