Projects per year
Search results
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Active
National Adrenoleukodystrophy (ALD) Registry
Gupta, A. O., Lund, T. C. & Orchard, P. J.
ASSOC OF PUBLIC HEALTH LABORATORIES, US Dept. of Health & Human Services HRSA
9/1/23 → 6/30/24
Project: Research project
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A Phase I Open Label Study to Evaluate the Safety andTolerability of ISP-001 in Patients with MucopolysaccharidosisType I
12/9/21 → 1/1/26
Project: Research project
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Engineered B Cells as a Universal Platform for the Treatment of Enzymopathies
Moriarity, B. S., Lund, T. C., McIvor, R. S., Orchard, P. J. & Webber, B. R.
NIH Nat'l Inst of Allergy & Infect Dis
3/1/20 → 2/28/25
Project: Research project
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Lysosomal Disease Network
Whitley, C. B., Ahmed, A., Braunlin, E. A., Cortez, D., Eisengart, J., King, K. E., Nestrasil, I. & Orchard, P. J.
NIH NAT INST OF NEURO DISORDERS & STROKE
9/15/19 → 7/31/25
Project: Research project
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Longterm Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
7/1/19 → 6/30/24
Project: Research project
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Finished
Collection of Sodium Heparin Plasma Samples from Subjects Undergoing Intravenous Busulfan Treatment
12/13/22 → 3/31/24
Project: Research project
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Mucopolysaccharidosis Newborn Screening meeting
ASSOC OF PUBLIC HEALTH LABORATORIES, US Dept. of Health & Human Services HRSA
8/23/22 → 9/30/23
Project: Research project
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Collection of Gene Mutations for Laboratory Quality AssuranceNewborn Screening Accuracy Project
SEQUOIA FOUNDATION, CENTERS FOR DISEASE CONTROL & PREVENTION
5/12/22 → 10/14/23
Project: Research project
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Lysosomal Storage Disease Focused Training
Orchard, P. J. & Miller, B. S.
11/8/21 → 11/7/23
Project: Research project
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Safety and efficacy of Nov340 delivery of SaRNA in treating MPS I disease
Whitley, C. B., Lund, T. C., Orchard, P. J. & Ou, L.
5/1/21 → 4/29/23
Project: Research project
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National Adrenoleukodystrophy (ALD) Registry
ASSOC OF PUBLIC HEALTH LABORATORIES, HRSA MATERNAL AND CHILD HEALTH (MCH)
11/26/20 → 8/31/23
Project: Research project
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Data on outcomes with allogenic haematopoietic stem cell transplants in Mucopolysaccharidosis type I
Orchard, P. J., Eisengart, J., Lund, T. C. & Miller, B. S.
9/9/20 → 5/6/22
Project: Research project
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Training for the Adult Subspecialist in Inherited Metabolic Disorders
Braunlin, E. A. & Orchard, P. J.
6/17/19 → 6/17/19
Project: Research project
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A Phase 3 Study of Lenti-D Drug Product After Myeloablative Conditioning Using Busulfan and Fludarabine in Subjects ≤ 17 Years of Age With Cerebral Adrenoleukodystrophy (CALD)
Orchard, P. J., Gupta, A. O., Kenney-Jung, D. L. & Lund, T. C.
2/1/19 → 1/31/24
Project: Research project
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Open-Label Phase 2 Pilot Study of Interferon Gamma-1b fo
Orchard, P. J. & Miller, W. P.
LUNDQUIST INSTITUTE FOR BIOMEDICAL INNO, HORIZON PHARMA
2/1/17 → 9/30/19
Project: Research project
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Discovery of brain MRI signatures in infants with severe
Nestrasil, I., Eberly, L., Elison, J. T., Mangia, S., Michaeli, S., Mueller, B. A., Orchard, P. J. & Svatkova, A.
5/1/16 → 4/30/18
Project: Research project
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Longitudinal study of bone and endocrine disease in chil
LUNDQUIST INSTITUTE FOR BIOMEDICAL INNO, GENZYME CORPORATION
1/1/16 → 4/26/18
Project: Research project
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Characterization of the Frequency and Function of CD4+ R
Orchard, P. J. & Miller, W. P.
UNITED LEUKODYSTROPHY FOUNDATION, INC.
1/1/16 → 5/1/18
Project: Research project
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MT2013-23R: Population Pharmacokinetics of Fludarabine i
UNIVERSITY OF CALIFORNIA, SAN FRANCISCO, NIH NAT'L CTR FOR ADVANCING TRAN SCIENCE
7/1/13 → 6/30/15
Project: Research project
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Pilot Study of Administration of Intravenous Laronidase
Orchard, P. J. & Polgreen, L.
9/19/11 → 6/19/18
Project: Research project
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NHLBI Production Assistance for Cellular Therapies (PACT
Wagner, J. E., Curtsinger, J. M., Hippen, K. L., Mc Cullough, J., McKenna, D. H., Miller, J. S. & Orchard, P. J.
NIH NAT'L HEART, LUNG, AND BLOOD INSTITU
1/15/10 → 1/14/15
Project: Research project
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CLINICAL TRIAL: PHASE II STUDY OF COMBINED LARONIDASE (ALDURAZYME) ENZYME REPLAC
National Center for Research Resources
12/1/08 → 11/30/09
Project: Research project
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Isoflavone-Mediated Glycosaminoglycan Reduction Therapy
Tolar, J., Charnas, L. & Orchard, P. J.
8/1/07 → 7/31/09
Project: Research project
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PHASE II STUDY OF COMBINED LARONIDASE (ALDURAZYME) ENZYME REPLACEMENT THERAPY (E
National Center for Research Resources
12/1/06 → 11/30/07
Project: Research project
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TRANSPLANTATION OF URB T CELLS CONTAINING THE HSV-TK SUICIDE GENE
National Center for Research Resources
12/1/05 → 11/30/06
Project: Research project
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PHASE II STUDY OF COMBINED LARONIDASE (ALDURAZYME) ENZYME REPLACEMENT THERAPY (E
National Center for Research Resources
12/1/05 → 11/30/06
Project: Research project
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Transplantation of URB T Cells Containing the HSV-TK Suicide Gene
National Center for Research Resources
12/1/03 → 11/30/04
Project: Research project
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TRANSPLANTATION OF URB T CELLS CONTAINING THE HSV-TK SUICIDE GENE
Balfour, J. J. & Orchard, P. J.
National Center for Research Resources
12/1/03 → 11/30/05
Project: Research project
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First International Symposium on Osteopetrosis:
National Institute of Arthritis and Musculoskeletal and Skin Diseases
9/1/03 → 8/31/04
Project: Research project
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GCRC-General Clinical Research Center
Dalmasso, A. A. P., Rocchini, A. P., Aldrich, N., Allen, S. S., Anderson, F. S., Macdonald, A. A. J., Dudek, A. A. Z., Matas, A. J., Leon, A. A. S., Sinaiko, A. A. R., Petryk, A., Moran, A. A. M., Bachanova, V. S., Berry, S. A., Kasiske, B. L., Van Ness, B. G., Hering, B. B. J., Karatekin, C., Torkelson, C. J., Earthman, C. P., Mariash, C. C. N., Verfaillie, C. C. M., Moldow, C. C., Nelson, C. A., Moldow, C. C. F., Chow, L. S., Gomez, C. M., Draheim, C. C., Kashtan, C., Jordan, C. C., Collins, T. C., Milla, C. C., Milla, C. C. E., Cheatham, C. C. L., Whitley, C. B., Fletcher, C. C. V., Kaiser, D. D., Johnson, D. D. Y., Duprez, D., Weisdorf, D. J., Canafax, D. D. M., Zelinskygoldman, D. D. A., Krason, D. D. A., Brown, D. D. M., Brown, D. D. R., Demerath, E. W., Treatjacobson, D. D. J., Neumark-sztainer, D. D. R., Donahue, C. B., Hunninghake, D. D. B., Dengel, D. R., Hatsukami, D. K., Pei, D. D., Gallaher, D. D., Hunter, D. D. J., Parks, E. E. J., Seaquist, E. R., Shapiro, E. G., Eugster, E. E. A., Giebink, G. G. S., Parry, G. G., Fulcher, G. G., Gaugler, J. E., Geller, M. A., Plotnikoff, G., Beilman, G. J., Gross, C. R., Metzger, G. G. J., Oz, G. G., Han, J. Y., Ibrahim, H. H. N., Hauff, L., Wynn, H. H., Wynnvezina, H. H., Hecht, S. S., Hongwanishkul, D., Balfour, H. H. H., Ikramuddin, S., Leppik, I. I. E., Baumgart, I. I., Redmon, J. J. B., Cloyd, J. J. C., White, J. J. G., Carey, J. R., Rank, J. J. M., Wozniak, J. J. R., Balfour, J. J., Billings, J. J. L., Slavin, J. J. L., Bloomfield, J. J., Bantle, J. J. P., Vuchetich, J. J. P., Day, J. J. W., Johnson, L. A. L., Dunitz, J. M., Pardo, J. V., Keenan, J. J., Gurney, J. J. G., Ahluwalia, J. J. S., Miller, J. J. B., Miller, J. J. S., Steinberger, J. J., Alavi, K. K., Daly, K. A., Thomas, K. K. M., Schmitz, K. K. H., Kehl, L., Skubitz, K. K. M., Lim, K. K. O., Baker, K. K. S., Khan, K. K. M., Kimberley, PT, T. J., Kirstein, M. N., Kurzer, M. S., Winters, K. K. C., Bushara, K. K. O., Allenberg, K. K., Sarafoglou, K. K., Stone, L. L. S., Downs, L. S., Carson, L. F., Burns, L. J., Halcon, L. L. L., Steffen, L. L. M., Lytle, L. A., Blumenthal, M. N., Hostetter, M. M., Hordinsky, M. K., Pereira, M. M. A., Mammel, M. C., Reding, M. M. T., Reicks, M. M., Hertz, M. I., Pylipow, M., Kennedy, M. M. B., Kushner, M. M., Kotlyar, M. M., Potegal, M., Steffes, M. W., Garwood, M. M. G., Mauer, M. M. S., Milev, P., Segall, M. M., Mooney, M. E., Mulrooney, D. A., Riches, M. M. L., Menge, M. M., Gunnar, M. M. R., Georgieff, M. M. K., Luciana, M. M., Al'absi, M. M. N., Gross, M. D., Nathan, B. M., Nazarian, S., Key, N. N., Nuttall, F. Q., Raymond, N. C., Key, N. N. S., Painter, P. L., Paller, M. S., Bauer, P. P. J., Faris, P. L., Yakshe, P. P., Orchard, P. J., Tuite, P. J., Pentel, P. R., Peterson, E. J., Petit, M. A., Polgreen, L. E., Jacobson, P. P. A., Regelmann, W. E., Miller, R. R., Gruetter, R., Remmel, R. P., Nagarajan, R. R., Grimm, R., Kempainen, R. R. R., Robertson, R. R. P., Schulz, S. S. C., Weisdorf, S. A., Schwarzenberg, S. J., Crow, S. S. J., Segal, B. M., Sibley, S., Specker, S. M., Smith, A. L., Sponheim, S. R., Straka, R. J., Raatz, S. S. K., Sutherland, D. E. R., Kumra, S., Cooley, S. S., Templeton, D. L., Terpstra, M. J., Therien, J. M., Sellers, T. T. A., Hostetter, T. T. H., Thomas, J. L., Whelan, T. T., Tracy, T. T. S., White, T., Schacker, T. W., Mathiowetz, V. G., Wagner, J. A., Walk, D., Warwick, W. W. J., Meller, W. H., Kennedy, W. W. R., Iacono, W. G., Yu, F., Balfour, H. H., Bantle, J. P., Barbosa, J. J., Blumenthal, M. N., Bouchard, T., Brown, D. M., Buchwald, H., Cavert, M. H., Chavers, B. M., Cloyd, J. C., Cohn, J. N., Daly, K., Day, J. W., Desnick, R. J., Dusenbery, K. E., Ferris, T. F., Fletcher, C. V., Frantz, I. D., Garwood, M. G., Goetz, F. C., Grimm, R. H., Gumnit, R. J., Halberg, F., Hatsukami, D. K., Hedemark, L. L., Hering, B. J., Hirsch, A. T., Hoogwerf, B. J., Hoogwerf, B. J., Hostetter, T. H., Hrushesky, W. J., Hrushesky, N. W. J., Hunninghake, D. B., Johnson, D. E., Kashtan, C. E., King, R. A., Klassen, A., Knopman, D. S., Kushner, M. G., Laine, D. C., Leon, A. S., Leppick, I. E., Leppik, I. E., Lippick, I., Luciana, M. M., Mariash, C. C. N., Matas, A. J., Mauer, M. S., Mauer, M. S., Messner, R. P., Michael, A. F., Miller, L. W., Miller, R. F., Miller, J. S., Mirkin, B. L., Mitchell, J. E., Moldrow, C. G., Monk, C. S., Moran, A. M., Oppenheimer, J. H., Page, A., Pereira, M. A., Pierpont, M. E. M., Raatz, S. K., Ralfour, H. H., Rank, J. M., Raymond, N. C., Redmon, J. B., Repka, T. L., Rhodus, N. L., Rice, K. L., Robertson, P. R., Roelofs, R., Schacker, T. W., Scheinman, J. I., Seaquist, E. R., Sharp, H. L., Sinaiko, A. R., Skubitz, K. M., Sofuoglu, M., Steffes, M. W., Steinberger, J., Sutherland, N. E. R., Sutherland, D. E. R., Taurog, J. D., Ulstrom, R. A., Vehe, R. K., Warwick, W. J., White, J. J. G., Whitley, C. B., Witkop, C. J., Young, T. L., Ziegler, R. J., Canafax, D. M., Crow, S. J., Eugster, E. A., Giebink, S. G., Jordan, C. M., Pentel, P. R., Sellers, T. A. & Verfaillie, C.
National Center for Research Resources
12/1/84 → 11/30/06
Project: Research project