Projects per year
Search results
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Active
Foundations for a Phase 1 clinical trial of cell-based therapy for Duchenne muscular dystrophy
Kang, P. B., Karachunski, P. I., Perlingeiro, R. & Wagner, J. E.
NIH NIAMS NATL INST OF ARTHRIT
7/15/22 → 6/30/24
Project: Research project
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A Prospective, Long Term Registry of Patients with a Diagnosis of Spinal Muscular Atrophy (SMA)
1/1/20 → 12/31/25
Project: Research project
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University of Minnesota Clinical Care Center
MUSCULAR DYSTROPHY ASSOCIATION
1/1/17 → 6/30/24
Project: Research project
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An Open-Label, Safety Study for Previously Treated
Karachunski, P. I., Day, J. W. & Raymond, G. V.
11/1/10 → 2/28/25
Project: Research project
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Finished
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Children and youth with special health needs care coordination quality improvement
5/1/19 → 10/31/20
Project: Research project
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A Prospective Non-interventional Study in Subjects with
Whitley, C. B. & Karachunski, P. I.
6/8/18 → 6/29/19
Project: Research project
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A phase 3 randomized, multicenter, multinational, double
Whitley, C. B., Karachunski, P. I. & Miller, B. S.
6/14/17 → 6/29/20
Project: Research project
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Probing the Activity of DUX4 in FSHD
NIH NIAMS NATL INST OF ARTHRIT
7/15/15 → 6/30/20
Project: Research project
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A PHASE 2 RANDOMIZED, DOUBLEBLIND, PLACEBO-CONTROLLED, M
Karachunski, P. I. & Raymond, G. V.
2/13/15 → 4/30/19
Project: Research project
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An Open-Label, Multi-Center, 48-Week Study with a Concur
Karachunski, P. I. & Raymond, G. V.
10/1/14 → 9/30/18
Project: Research project
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Prosensa-An open-label extension study of the long-term
Raymond, G. V. & Karachunski, P. I.
9/1/14 → 10/30/16
Project: Research project
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MDA Travel Support for FOR-DMD Project
UNIVERSITY OF ROCHESTER, MUSCULAR DYSTROPHY ASSOCIATION
10/1/13 → 9/30/14
Project: Research project
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Establishing Minimal Clinically Important Differences
CHILDREN'S RESEARCH INSTITUTE, U.S. DEPARTMENT OF DEFENSE
9/30/12 → 9/29/15
Project: Research project
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CINRG Study Specific Agreement 01 - "Clinical Meaningful
CHILDREN'S RESEARCH INSTITUTE, NIH NIAMS NATL INST OF ARTHRIT
9/1/12 → 8/31/15
Project: Research project
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Clinical Meaningful Outcomes for Duchenne Muscular Dystr
CHILDREN'S RESEARCH INSTITUTE, PARENT PROJECT MUSCULAR DYSTROPHY
9/1/12 → 8/31/14
Project: Research project
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NIH/NIAMS 1R01AR062380 Biomarkers Discovery and Validati
CHILDREN'S RESEARCH INSTITUTE, NIH NIAMS NATL INST OF ARTHRIT
9/1/12 → 8/31/15
Project: Research project
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CINRG Study Specific Agreement 04 - "Center for Research
CHILDREN'S RESEARCH INSTITUTE, NIH NIAMS NATL INST OF ARTHRIT
9/1/12 → 8/31/15
Project: Research project
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PITT0112: Becker Muscular Dystrophy A Natural History
Manousakis, G. E. & Karachunski, P. I.
CHILDREN'S RESEARCH INSTITUTE, NIH NIAMS NATL INST OF ARTHRIT
9/1/12 → 8/31/18
Project: Research project
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FOR-DMD: Double-Blind Randomized Trial of Optimize Stero
UNIVERSITY OF ROCHESTER, NIH NAT INST OF NEURO DISORDERS & STROKE
7/1/12 → 6/30/14
Project: Research project
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Optimization of Human iPS- Based Cell Therapy for Muscular Dystrophies
National Institute of Arthritis and Musculoskeletal and Skin Diseases
7/1/12 → 6/30/14
Project: Research project
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A Multicenter Collaborative Study on the Clinical Featur
CHILDREN'S RESEARCH INSTITUTE, FSH SOCIETY, INC.
3/2/12 → 2/28/15
Project: Research project
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Clinical Outcome Validation in Non-Ambulatory and Young
WASHINGTON UNIVERSITY IN ST. LOUIS, MUSCULAR DYSTROPHY ASSOCIATION
1/1/12 → 12/31/12
Project: Research project
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Bone Health in Duchenne Muscular Dystrophy
FRANK J AND ELEANOR A MASLOWSKI CH TRUST
1/1/12 → 6/30/15
Project: Research project
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Structural and Functional CNS Changes in Myotonic Dystro
Karachunski, P. I., Hemmy, L. S., Lim, K. O. & Wozniak, J. R.
STANFORD UNIVERSITY, NIH NAT INST OF NEURO DISORDERS & STROKE
9/1/11 → 3/31/13
Project: Research project
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Muscular Dystrophy Center Core Laboratories
Ervasti, J. M., Perrin, B. J., Day, J. W., Karachunski, P. I., Darabi, R. & Thomas, D. D.
National Institute of Arthritis and Musculoskeletal and Skin Diseases
8/1/09 → 12/30/14
Project: Research project
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Treatment of the Dystrophin Deficient Cardiomyopathy
Karachunski, P. I., Braunlin, E. A., Kochilas, L. & Day, J. W.
NATIONWIDE CHILDREN'S HOSPITAL, MUSCULAR DYSTROPHY ASSOCIATION
7/1/09 → 6/30/12
Project: Research project
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A Phase 2b Efficacy and Safety Study of PTC124 in Subjec
Day, J. W. & Karachunski, P. I.
3/1/08 → 2/28/12
Project: Research project
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Myozyme Temporary Access Program (MTAP)
Day, J. W. & Karachunski, P. I.
8/31/07 → 8/30/10
Project: Research project
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A Placebo Controlled, Randomized, Double-Blind Phase II
Day, J. W. & Karachunski, P. I.
8/23/07 → 8/22/11
Project: Research project
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Clinical Neuromuscular Training Grant
MUSCULAR DYSTROPHY ASSOCIATION
7/1/06 → 6/30/08
Project: Research project
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Comparative efficacy of three doses of intravenous immun
Karachunski, P. I. & Muley, S.
3/1/06 → 12/31/12
Project: Research project