A Phase 1/2, open-label, dose escalation study to evaluate the safety and efficacy of mRNA-3704 in patients with isolated methylmalonic acidemia (MMA) due to MUT deficiency

Project: Research project

Project Details

Description

A Phase 1/2, open-label, dose escalation study to evaluate the safety and efficacy of mRNA-3704 in patients with isolated methylmalonic acidemia (MMA) due to MUT deficiency
StatusFinished
Effective start/end date2/1/209/10/21

Funding

  • MODERNATX, INC.

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