An Open-label, Phase 1/2 Study to Evaluate the Safety and Efficacy of Single-dose PR001A in Infants with Type 2 Gaucher Disease

Project: Research project

Project Details

Description

An Open-label, Phase 1/2 Study to Evaluate the Safety and Efficacy of Single-dose PR001A in Infants with Type 2 Gaucher Disease
StatusActive
Effective start/end date9/8/201/1/26

Funding

  • PREVAIL THERAPEUTICS INC

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