Long-term outcomes of systemic therapies for Hurler syndrome: an international multicenter comparison

Julie B. Eisengart, Kyle D. Rudser, Yong Xue, Paul Orchard, Weston Miller, Troy Lund, Ans Van der Ploeg, Jean Mercer, Simon Jones, Karl Eugen Mengel, Seyfullah Gökce, Nathalie Guffon, Roberto Giugliani, Carolina F.M. de Souza, Elsa G. Shapiro, Chester B. Whitley

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