Network
University of Minnesota
Organizational unit: University
Liberal Arts Technologies and Innovation Services
Organizational unit: Department
Medical University of South Carolina
External organization: Academic
Boston Children's Hospital
External organization: Medical
Northwestern University
External organization: Academic
University of Minnesota Twin Cities
External organization: Academic
National Institutes of Health
External organization: Government
Stanford University
External organization: Academic
Department of Veterans Affairs
External organization: Government
Columbus Children's Hospital
External organization: Unknown
Children's Memorial Hospital
External organization: Medical
The Ohio State University
External organization: Academic
Harvard University
External organization: Academic
Johns Hopkins University
External organization: Academic
Novartis Gene Therapies Inc.
External organization: Unknown
University of Montreal
External organization: Academic
Great Ormond Street Hospital for Children NHS Trust
External organization: Medical
Primary Children's Medical Center
External organization: Medical
National Institute of Child Health and Human Development
External organization: Unknown
Novartis Pharmaceuticals
External organization: Unknown
University College London
External organization: Academic
Slaney Family Fund
External organization: Unknown
Catholic University of the Sacred Heart
External organization: Academic
Sarepta Pharmaceuticals
External organization: Unknown
University of North Carolina
External organization: Academic
Boston College
External organization: Academic
University of Copenhagen
External organization: Academic
Michigan State University
External organization: Academic
Neuroscience Institute
External organization: Unknown
Ball Aerospace and Technologies Corp.
External organization: Corporate
AveXis
External organization: Unknown
University of Alabama
External organization: Academic
Abigial Spoden
External organization: Unknown
Cure SMA Industry Collaboration
External organization: Unknown
Newtown Square
External organization: Unknown
National Institutes of Health
External organization: Unknown
Cytokinetics
External organization: Unknown
St. Jude Children Research Hospital
External organization: Medical
Rowan University
External organization: Academic
McGill University
External organization: Unknown
National Institute of Diabetes and Digestive and Kidney Diseases
External organization: Unknown
Danish Parkinson’s Foundation
External organization: Unknown
Newcastle upon Tyne Hospitals NHS Foundation Trust
External organization: Medical
Tandlægeforeningen
External organization: Unknown
Muscular Dystrophy Association
External organization: Unknown
Kay Square Scientific
External organization: Unknown
Biogen IDEC
External organization: Corporate
Novartis Gene Therapies
External organization: Unknown
University of Rochester
External organization: Academic
Inc.
External organization: Unknown
National Institute on Deafness and Other Communication Disorders (NIDCD)
External organization: Unknown
Charlotte Eye Ear Nose and Throat Associates
External organization: Unknown
Department of Anatomy & Neurobiology
External organization: Unknown
BIOPAC Systems, Inc.
External organization: Unknown
National Institute of Environmental Health Sciences
External organization: Unknown
Evelina London Children's Hospital
External organization: Unknown
Inc.
External organization: Unknown
Centro Clinico Nemo
External organization: Unknown
Ionis Pharmaceuticals
External organization: Unknown
Novartis Gene Therapies, Inc.
External organization: Unknown
National Rehabilitation Centre for Neuromuscular Diseases
External organization: Unknown
National Institute of Neurological Disorders and Stroke
External organization: Unknown
Spinal Muscular Atrophy Foundation
External organization: Unknown
Utrecht University
External organization: Academic
Northeastern University
External organization: Academic
PTC Therapeutics
External organization: Unknown
U.S. DEPARTMENT OF VETERANS AFFAIRS
External organization: Primary Sponsor
CureSMA
External organization: Unknown
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
External organization: Medical