Medicine & Life Sciences
Mucopolysaccharidosis I
100%
Mucopolysaccharidosis II
44%
Mucopolysaccharidoses
39%
Gangliosidoses
33%
Longitudinal Studies
26%
TimeLine
25%
Caregivers
24%
Enzyme Replacement Therapy
18%
Mucopolysaccharidosis VI
15%
Mucopolysaccharidosis III
15%
Phenotype
15%
Adrenoleukodystrophy
14%
Distance Education
13%
Corpus Callosum
13%
Hematopoietic Stem Cell Transplantation
13%
Emotional Adjustment
12%
Enzymes
12%
Learning
11%
GM2 Gangliosidosis
10%
Erythropoietin
10%
GM1 Gangliosidosis
10%
Natural History
10%
Child
9%
Transplants
9%
Parents
8%
Therapeutics
8%
miglustat
8%
Cognitive Dysfunction
8%
Quality of Life
8%
Language
7%
Cerebrospinal Fluid
7%
Neurodegenerative Diseases
7%
Pandemics
6%
Health Care Outcome Assessment
6%
Iduronidase
6%
Placebos
6%
Randomized Controlled Trials
6%
Biomarkers
6%
Aptitude
6%
Blood Pressure
6%
Video Recording
6%
Brain
5%
Walking
5%
Gestational Age
5%
Mutation
5%
Sandhoff Disease
5%
Central Nervous System
5%
Kidney
5%
Tay-Sachs Disease
5%