Optimizing the transduction efficiency of capsid-modified AAV6 serotype vectors in primary human hematopoietic stem cells in vitro and in a xenograft mouse model in vivo

Liujiang Song, M. Ariel Kauss, Etana Kopin, Manasa Chandra, Taihra Ul-Hasan, Erin Miller, Giridhara R. Jayandharan, Angela E. Rivers, George V. Aslanidi, Chen Ling, Baozheng Li, Wenqin Ma, Xiaomiao Li, Lourdes M. Andino, Li Zhong, Alice F. Tarantal, Mervin C. Yoder, Kamehameha K. Wong, Mengqun Tan, Saswati ChatterjeeArun Srivastava

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Medicine & Life Sciences